United States Genetic Disorder Drugs Research

Major Players: AbbVie Inc , Gilead Sciences, Inc, Mylan N.V, Alaxia, Vertex Pharmaceuticals Incorporated

Major Players: Amicus Therapeutics, EpiVax, Inc, Sanofi Inc., AVROBIO, Inc., Astellas Pharma

Major Players: Bayer AG, Pfizer, Inc., Takeda Pharmaceutical Co. Ltd., Sanofi S.A, Novo Nordisk

Major Players: Pfizer, Inc., Bayer AG, Novo Nordisk A/S, CSL Limited (CSL Behring), BioMarin

Major Players: Bluebird Bio, Novartis AG, ApoPharma Inc, Bellicum Pharmaceuticals, Pfizer, Inc.

Major Players: CSL Behring, Grifols, S.A., Takeda Pharmaceutical Company Ltd, Octapharma AG, Bio Products Laboratory Ltd.

Major Players: CSL Behring, Takeda Pharmaceutical Company Limited, Pharming Healthcare Inc., Sanofi, BioCryst Pharmaceuticals Inc.

Major Players: NIPPON SHINYAKU CO., LTD. (NS Pharma Inc.), ITALFARMACO S.p.A., PTC Therapeutics, Santhera Pharmaceuticals, Sarepta Therapeutics

Major Players: Novartis AG, Emmaus Medical Inc., Addmedica, Medunik USA Inc., Global Blood Therapeutics Inc

Major Players: AstraZeneca plc, Clovis Oncology, Pfizer Inc., Onxeo, GSK plc

Major Players: Pfizer, Inc., Alnylam Pharmaceuticals Inc., Teva Pharmaceutical Industries Ltd., Neurocrine Biosciences, Inc., Ionis Pharmaceuticals

Major Players: REGENXBIO Inc., Clinigen Group plc, JCR Pharmaceuticals, ArmaGen, Takeda Pharmaceutical Company Limited (Shire)

Major Players: Sanofi (Genzyme Corporation), Takeda Pharmaceutical Company Limited, Amicus Therapeutics, Inc, ISU ABXIS, JCR Pharmaceuticals Co., Ltd.

Major Players: Sanofi S.A., Global Blood Therapeutics, Inc., bluebird bio, Inc., EMI Holding, Inc., Celgene Corporation