Pompe Disease Top Companies
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Amicus Therapeutics
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Sanofi
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Exerkine Corporation
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Genethon
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Maze Therapeutics, Inc.
*Disclaimer: Top companies sorted in no particular order
Pompe Disease Market Concentration
Pompe Disease Company List
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Sanofi
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Amicus Therapeutics
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Astellas Pharma / Audentes
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Asklepios BioPharmaceutical (AskBio)
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Genethon
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Orchard Therapeutics
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Shionogi & Co., Ltd.
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Beijing GeneCradle Technology Co., Ltd.
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Maze Therapeutics, Inc.
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Exerkine Corporation