Lysosomal Storage Disease Treatment Top Companies
Pfizer
Takeda Pharmaceuticals
Sanofi
BioMarin
Johnson & Johnson
*Disclaimer: Top companies sorted in no particular order

Lysosomal Storage Disease Treatment Market Concentration

Lysosomal Storage Disease Treatment Company List
Sanofi
Takeda Pharmaceuticals
Pfizer
BioMarin
Johnson & Johnson
Amicus Therapeutics
Alexion Pharmaceuticals
Sigilon Therapeutics
GC Biopharma
Orchard Therapeutics
Cyclo Therapeutics
IntraBio
Chiesi Farmaceutici
Freeline Therapeutics
Rocket Pharmaceuticals
Forge Biologics
Polaryx Therapeutics
M6P Therapeutics
Sarepta Therapeutics
Krystal Biotech


